Neonatal Screening for Spinal Muscular Atrophy and Severe T- and B-Cell Lymphopenias in Andalusia: A Prospective Study.

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Tác giả: Pilar Blanco-Lobo, Rocio Castro-Serrano, Beatriz De Felipe, Carmen Delgado-Pecellin, Cristina Duque, Raquel M Fernandez, Mercedes Lopez-Lobato, Jose M Lucena, Marcos Madruga-Garrido, Josefina Marquez-Fernandez, Beatriz Mendoza, Mariana Moreno-Prieto, Olaf Neth, Peter Olbrich, Maria Ruiz-Camacho, Carmen Salamanca, Alberto Varona

Ngôn ngữ: eng

Ký hiệu phân loại: 391.412 Gloves and mittens

Thông tin xuất bản: Switzerland : International journal of neonatal screening , 2025

Mô tả vật lý:

Bộ sưu tập: NCBI

ID: 252058

 Spinal muscular atrophy (SMA) and severe T- and/or B-cell lymphopenias (STBCL) in the form of severe combined immunodeficiencies (SCID) or X-linked agammaglobulinemia (XLA) are rare but potentially fatal pathologies. In January 2021, we initiated the first pilot study in Spain to evaluate the efficacy of a very early detection technique for SMA and SCID. RT-PCR was performed on prospectively collected dried blood spots (DBSs) from newborns in Western Andalusia (Spain). Internal and external controls (SCID, XLA and SMA) were included. The determination of SMA was relative (positive/negative) and that of TRECs and KRECs was quantitative (copies/punch). A total of 14.035 prospective samples were analysed. All controls were correctly identified while no cases of SMA or SCID/XLA were prospectively identified. DBS analysis of infants with suspected SMA or STBCL that presented to our centre showed pathological values in two cases each for SMA and SCID and one for XLA, all of them being subsequently confirmed genetically. In this prospective pilot study, no infants with SMA or STBCL were detected
  however, the technique applied here was shown to be reliable and fast, further supporting the benefits and need to include SMA and SCID in national newborn screening (NBS) programs, as it will allow early supportive and curative therapy.
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