Loại tài liệu:    Chỉ tìm trong: 
101-106 trong số 106 kết quả
Sodium valproate, a potential repurposed treatment for the neurodegeneration in Wolfram syndrome (TREATWOLFRAM): trial p...
Tác giả: Renuka P Dias, Kristian Brock, Archana Kulkarni, Isabelle Meunier, Lucinda Billingham, Zsuzsanna Nagy, Heather Rose, Sulev Koks, Malgorzata Zatyka, Dewi Astuti, Tracy Lynch, Karen E Morrison, Kun Hu, Darren Barton, Sabrina Cronier, Rebecca Malpass, Ruth Evans, Amandip Malhi, Pooja Takhar, Amy Lamb, Gema Esteban-Bueno, Wojciech Młynarski, Christophe Orssaud, Rajat Gupta, Agathe Roubertie, Victoria Homer, Timothy Barrett, Una Martin, Andrew Peet, Martin Wilson, Patrick Yu-Wai-Man, Benjamin Wright, Susan Mollan
Xuất bản: England: BMJ open , 2025
Bộ sưu tập: NCBI
ddc: 
 
The EU project Real4Reg: unlocking real-world data with AI
Tác giả: Jonas Peltner, Cornelia Becker, Monika Roberta Korcinska Handest, Manuel Lentzen, Peggy Maguire, Niels Henrik Meedom, Rebecca Moore, Vanessa Moore, Dávid Nagy, Hillary McNamara, Anne Paakinaho, Kerstin Pfeifer, Julia Wicherski, Liisa Pylkkänen, Blair Rajamaki, Evy Reviers, Christoph Röthlein, Martin Russek, Célia Silva, Dirk De Valck, Thuan Vo, Elvira Bräuner, Holger Fröhlich, Silja Wortberg, Cláudia Furtado, Sirpa Hartikainen, Aleksi Kallio, Anna-Maija Tolppanen, Britta Haenisch, Mohamed Aborageh, Inês Costa, Vera Ehrenstein, Joana Fernandes, Steffen Heß, Erzsébet Horváth-Puhó
Xuất bản: England: Health research policy and systems , 2025
Bộ sưu tập: NCBI
ddc: 
 
High-efficiency base editing in the retina in primates and human tissues
Tác giả: Alissa Muller, Jack Sullivan, Simon Manuel Hostettler, Patricia Galliker, Yanyan Hou, Pierre Balmer, Tamás Virág, Luis Alberto Barrera, Lauren Young, Quan Xu, Dániel Péter Magda, Ferenc Kilin, Wibke Schwarzer, Arogya Khadka, Pierre-Henri Moreau, Lyne Fellmann, Thierry Azoulay, Mathieu Quinodoz, Duygu Karademir, Juna Leppert, Alex Fratzl, Georg Kosche, Ruchi Sharma, Mantian Wang, Jair Montford, Marco Cattaneo, Mikaël Croyal, Therese Cronin, Simone Picelli, Alice Grison, Cameron S Cowan, Ákos Kusnyerik, Philipp Anders, Magdalena Renner, Cindy Park-Windhol, Zoltán Zsolt Nagy, Arnold Szabó, Kapil Bharti, Carlo Rivolta, Hendrik P N Scholl, David Bryson, Giuseppe Ciaramella, Botond Roska, Bence György, Pascal W Hasler, Lucas Janeschitz-Kriegl, Mert Duman, Beryll Klingler, Jane Matsell
Xuất bản: United States: Nature medicine , 2025
Bộ sưu tập: NCBI
ddc: 
 
High-efficiency base editing in the retina in primates and human tissues
Tác giả: Alissa Muller, Jack Sullivan, Simon Manuel Hostettler, Patricia Galliker, Yanyan Hou, Pierre Balmer, Tamás Virág, Luis Alberto Barrera, Lauren Young, Quan Xu, Dániel Péter Magda, Ferenc Kilin, Wibke Schwarzer, Arogya Khadka, Pierre-Henri Moreau, Lyne Fellmann, Thierry Azoulay, Mathieu Quinodoz, Duygu Karademir, Juna Leppert, Alex Fratzl, Georg Kosche, Ruchi Sharma, Mantian Wang, Jair Montford, Marco Cattaneo, Mikaël Croyal, Therese Cronin, Simone Picelli, Alice Grison, Cameron S Cowan, Ákos Kusnyerik, Philipp Anders, Magdalena Renner, Cindy Park-Windhol, Zoltán Zsolt Nagy, Arnold Szabó, Kapil Bharti, Carlo Rivolta, Hendrik P N Scholl, David Bryson, Giuseppe Ciaramella, Botond Roska, Bence György, Pascal W Hasler, Lucas Janeschitz-Kriegl, Mert Duman, Beryll Klingler, Jane Matsell
Xuất bản: United States: Nature medicine , 2025
Bộ sưu tập: NCBI
ddc: 
 
Molecular Profiling Reveals Novel Gene Fusions and Genetic Markers for Refined Patient Stratification in Pediatric Acute...
Tác giả: Borbála Péterffy, Szilvia Krizsán, Anna Bekő, Lili Anna Kenéz, Zsuzsanna Jakab, György Péter, Marianna Zombori, Krisztina Csanádi, Gábor Ottóffy, Katalin Csernus, Ágnes Vojcek, Lilla Györgyi Tiszlavicz, Bálint Egyed, Krisztina Mita Gábor, Ágnes Kelemen, Péter Hauser, Krisztián Kállay, Gabriella Kertész, Zsuzsanna Gaál, István Szegedi, Gábor Barna, Ágnes Márk, Irén Haltrich, Gábor Bedics, Zsuzsanna Hevessy, Anikó Ujfalusi, Béla Kajtár, Botond Timár, Csongor Kiss, Gergely Kriván, András Matolcsy, Suvi Savola, Gábor Kovács, Csaba Bödör, Anne Benard-Slagter, Donát Alpár, Sander Palit, Dániel János Erdélyi, Judit Müller, Tibor Nagy, Lajos László Hegyi
Xuất bản: United States: Modern pathology : an official journal of the United States and Canadian Academy of Pathology, Inc , 2025
Bộ sưu tập: NCBI
ddc: 
 
Semaglutide and Nonarteritic Anterior Ischemic Optic Neuropathy
Tác giả: Cindy X Cai, Michelle Hribar, Aiyin Chen, Sophia Wang, Cecilia Lee, Theodore Leng, Joshua R Ehrlich, Andrew Barkmeier, Karen R Armbrust, Michael V Boland, David Dorr, Danielle Boyce, Sally Baxter, Thamir Alshammari, Joel Swerdel, Marc A Suchard, Martijn Schuemie, Fan Bu, Anthony G Sena, George Hripcsak, Akihiko Nishimura, Paul Nagy, Thomas Falconer, Kerry Goetz, Scott L DuVall, Michael Matheny, Benjamin Viernes, William O'Brien, Linying Zhang, Benjamin Martin, Erik Westlund, Nestoras Mathioudakis, Ruochong Fan, Adam Wilcox, Swarup S Swaminathan, Albert Lai, Jacqueline C Stocking, Sahar Takkouche, Lok Hin Lee, Yangyiran Xie, Izabelle Humes, David B McCoy, Mohammad Adibuzzaman, Raymond G Areaux, William Rojas-Carabali, Alexis Flowers, James Brash, David A Lee, Nicole G Weiskopf, Louise Mawn, Rupesh Agrawal, Hannah Morgan-Cooper, Priya Desai, Patrick B Ryan, Eric N Brown, Brian Toy, Benjamin Xu, John Chen
Xuất bản: United States: JAMA ophthalmology , 2025
Bộ sưu tập: NCBI
ddc: 
 

Truy cập nhanh danh mục