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Tìm được 40 kết quả
Long-term efficacy and safety of danicopan as add-on therapy to ravulizumab or eculizumab in PNH with significant EVH
Tác giả: Austin Kulasekararaj, Morag Griffin, Yogesh Patel, Peng Liu, Gleb Filippov, Flore Sicre de Fontbrune, Antonio Risitano, Jong Wook Lee, Caroline Piatek, Jamile Shammo, Jun-Ichi Nishimura, Christopher Patriquin, Hubert Schrezenmeier, Wilma Barcellini, Jens Panse, Anna Gaya
Xuất bản: United States: Blood , 2025
Bộ sưu tập: NCBI
ddc:  627.12
 
BRAFV600E induces key features of LCH in iPSCs with cell type-specific phenotypes and drug responses
Tác giả: Giulio Abagnale, Raphaela Schwentner, Florian Halbritter, Martin Distel, Sebastian K Eder, Caroline Hutter, Philipp Ben Soussia-Weiss, Wouter van Midden, Caterina Sturtzel, Ulrike Pötschger, Magdalena Rados, Sabine Taschner-Mandl, Ingrid Simonitsch-Klupp, Christoph Hafemeister
Xuất bản: United States: Blood , 2025
Bộ sưu tập: NCBI
ddc:  271.6
 
Defining pathogenic IL-17 and CSF-1 gene expression signatures in chronic graft-versus-host disease
Tác giả: Julie R Boiko, Kathleen S Ensbey, Stephanie J Lee, Scott N Furlan, Geoffrey R Hill, Olivia G Waltner, Isaac C Jenkins, Shruti S Bhise, Kelli Pa MacDonald, Bruce R Blazar, Anne Marcie Hall, Ted A Gooley, Simone A Minnie
Xuất bản: United States: Blood , 2025
Bộ sưu tập: NCBI
ddc:  363.232
 
Surface pTα expression predicts LCK activation and preclinical synergy of LCK and JAK coinhibition in adult T-ALL
Tác giả: Lucien Courtois, Antoine Pinton, Grégoire Huré, Nicolas Gaidot, Elizabeth A Macintyre, Hervé Dombret, André Baruchel, Nicolas Boissel, Aurore Touzart, Ludovic Lhermitte, Philippe Rousselot, Vahid Asnafi, Aurelie Cabannes-Hamy, Mathieu Simonin, Guillaume P Andrieu, Mélodie Queri, Charlotte Smith, Guillaume Charbonnier, Marie-Emilie Dourthe, Marianne Courgeon
Xuất bản: United States: Blood , 2025
Bộ sưu tập: NCBI
ddc:  912.01
 
Therapeutic switch from plasma to recombinant ADAMTS13 for patients with congenital TTP from Japanese real-world data
Tác giả: Kazuya Sakai, Atsushi Hamamura, Masahiro Takeyama, Teruhisa Taoka, Naoki Fujita, Minoru Kanaya, Katsuyoshi Koh, Hiroshi Shiragami, Hidekazu Azumi, Kenki Saito, Masanori Matsumoto, Yoshiko Yoshimura, Miyuki Abe, Yoshiyuki Ogawa, Kazuki Tanaka, Norimichi Hattori, Tazuko Tokugawa, Rie Kanai, Fumiyoshi Ikejiri
Xuất bản: United States: Blood , 2025
Bộ sưu tập: NCBI
ddc:  373.236
 
Biology as vulnerability in follicular lymphoma: genetics, epigenetics, and immunogenetics
Tác giả: Ferran Araujo-Ayala, Wendy Béguelin
Xuất bản: United States: Blood , 2025
Bộ sưu tập: NCBI
ddc: 
 
Ruxolitinib combined with dexamethasone for adult patients with newly diagnosed hemophagocytic lymphohistiocytosis in Ch...
Tác giả: De Zhou, Xianbo Huang, Jingjing Zhu, Shuqi Zhao, Wanzhuo Xie, Hongyan Tong, Jie Jin, Xiujin Ye, Lixia Zhu, Xuelian Hu, Xiudi Yang, Mixue Xie, Xin Huang, Fang Yu, Juying Wei, Liya Ma
Xuất bản: United States: Blood , 2025
Bộ sưu tập: NCBI
ddc: 
 
Single-cell panleukemia signatures of HSPC-like blasts predict drug response and clinical outcome
Tác giả: Changya Chen, Jason Xu, Elizabeth Y Li, Austin Yang, Xiaohuan Qin, Shovik Bandyopadhyay, Jacqueline Jiahui Peng, Petri Pölönen, Haley Newman, Brent Wood, Jianzhong Hu, Rawan Shraim, Jonathan H Sussman, Andrew D Hughes, Caroline Diorio, Lahari Uppuluri, Gongping Shi, Theresa Ryan, Tori Fuller, Mignon L Loh, Elizabeth A Raetz, Stephen P Hunger, Stanley B Pounds, Tiffaney L Vincent, Charles G Mullighan, David Frank, Jun J Yang, Kathrin Maria Bernt, David Trent Teachey, Kai Tan, Joseph S Tumulty, Satoshi Yoshimura, Fatemeh Alikarami, Wenbao Yu, Yang-Yang Ding, Chia-Hui Chen
Xuất bản: United States: Blood , 2025
Bộ sưu tập: NCBI
ddc: 
 
Beyond genotype: challenges in predicting disease risk for carriers of biallelic perforin variants
Tác giả: Oliver Wegehaupt, Oleg Borisov, Despina Moshous, Geneviève de Saint Basile, Wenying Zhang, Rebecca A Marsh, Carmela De Fusco, Katharina Wustrau, Fabio Timeus, Concetta Micalizzi, Eberhard Gunsilius, Laine Hosking, Elena Sieni, Sharon Choo, Sujal Ghosh, Anna Köttgen, Kai Lehmberg, Stephan Ehl, Florian Oyen, Jasmin Mann, Maria Luisa Coniglio, Aurora Chinnici, Francesco Pegoraro, Linda Beneforti, Kimberly C Gilmour
Xuất bản: United States: Blood , 2025
Bộ sưu tập: NCBI
ddc:  297.1248
 
Pathogenesis of Paroxysmal Nocturnal Hemoglobinuria
Tác giả: Lucio Luzzatto, Shinji Nakao
Xuất bản: United States: Blood , 2025
Bộ sưu tập: NCBI
ddc:  658.32259
 
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