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21-30 trong số 378 kết quả
Beyond genotype: challenges in predicting disease risk for carriers of biallelic perforin variants
Tác giả: Oliver Wegehaupt, Oleg Borisov, Despina Moshous, Geneviève de Saint Basile, Wenying Zhang, Rebecca A Marsh, Carmela De Fusco, Katharina Wustrau, Fabio Timeus, Concetta Micalizzi, Eberhard Gunsilius, Laine Hosking, Elena Sieni, Sharon Choo, Sujal Ghosh, Anna Köttgen, Kai Lehmberg, Stephan Ehl, Florian Oyen, Jasmin Mann, Maria Luisa Coniglio, Aurora Chinnici, Francesco Pegoraro, Linda Beneforti, Kimberly C Gilmour
Xuất bản: United States: Blood , 2025
Bộ sưu tập: NCBI
ddc:  621.982
 
Pathogenesis of Paroxysmal Nocturnal Hemoglobinuria
Tác giả: Lucio Luzzatto, Shinji Nakao
Xuất bản: United States: Blood , 2025
Bộ sưu tập: NCBI
ddc:  296.1121
 
Proteostasis Disruption in Inherited Bone Marrow Failure Syndromes
Tác giả: Helena Yu, Robert Signer
Xuất bản: United States: Blood , 2025
Bộ sưu tập: NCBI
ddc:  332.456091
 
Impact of HLA Alloimmunization in Gene-Modified Autologous Stem Cell Transplant For Transfusion-Dependent Thalassemia
Tác giả: Nora M Gibson, Eugene Khandros, Caitlin W Elgarten, Elizabeth Worster, Dimitrios S Monos, Alexis A Thompson, Janet L Kwiatkowski, Timothy Olson
Xuất bản: United States: Blood , 2025
Bộ sưu tập: NCBI
ddc:  612.665
 
Blunted CD40-responsive enhancer activation in CREBBP-mutant lymphomas can be restored by enforced CD4 T-cell engagement
Tác giả: Haopeng Yang, Wenchao Zhang, Sydney Parsons, Ariel Mechaly, Leslie Regad, Ahmed Haouz, Christopher R Flowers, Sattva S Neelapu, Loretta J Nastoupil, Richard Eric Davis, Qing Deng, Fernando Rodrigues Lima, Vida Ravanmehr, Michael R Green, Guiling Cui, Kevin Bowman, Ruidong Chen, Jared Henderson, Shyanne Ruby Lockman, Estela Rojas, Ashley Lauren Wilson
Xuất bản: United States: Blood , 2025
Bộ sưu tập: NCBI
ddc:  296.185
 
Itacitinib for the Prevention of IEC Therapy-Associated CRS: Results From the Two-Part Phase 2 INCB 39110-211 Study
Tác giả: Matthew J Frigault, Richard T Maziarz, Jing Lei, Michael Pratta, Rodica Morariu-Zamfir, John F DiPersio, Jae H Park, Aleksandr Lazaryan, Nirav N Shah, Jakub Svoboda, Lazaros J Lekakis, Ran Reshef, Christine L Phillips, Lea Burke
Xuất bản: United States: Blood , 2025
Bộ sưu tập: NCBI
ddc:  553.453
 
HLA-haploidentical stem cell transplantation for chronic granulomatous disease: an EBMT-IEWP retrospective study
Tác giả: Quentin Riller, Mathias M Hauri-Hohl, Fulvio Porta, Benedicte Bruno, Marco Zecca, Serap Aksoylar, Vincent Barlogis, Catharina Schuetz, Jochen Buechner, Maura Faraci, Claudia Wehr, Wolfgang Holter, Su Han Lum, Karin M Mellgren, Franco Locatelli, Antonio Pérez-Martínez, Felipe Suarez, Despina Moshous, Andrew R Gennery, Dmitry Balashov, Michael H Albert, Mary A Slatter, Tayfun Güngör, Jeroen Knippenberg, Bénédicte Neven, Tiarlan Sirait, Alexandra Laberko, Khalid Halahleh, Hasan Hashem, Musa Karakukcu, Henrik Sengeloev
Xuất bản: United States: Blood , 2025
Bộ sưu tập: NCBI
ddc:  383.14
 
The neutrophil antigen 3a/b polymorphism in SLC44A2 unexpectedly encodes Csa/Csb red cell antigens
Tác giả: Romain Duval, Alissa Soudry, Damien Vainqueur, Jérôme Babinet, Cécile Masson, Jean Christophe Gelly, Caroline Le Van Kim, Marc Romana, Dawei Chen, Sentot Santoso, Berengere Koehl, Thierry Peyrard, Jonathan De Oliveira Rios, Slim Azouzi, Sarah Liane Linguet, Miguel Taillepierre, Graziella Matesic, Alexandre Raneri, Guy Laiguillon, Emilie Le Toriellec, Emilie-Fleur Gautier
Xuất bản: United States: Blood , 2025
Bộ sưu tập: NCBI
ddc:  571.9677
 
A TIM-3-Fc decoy secreted by engineered T cells improves CD19 CAR-T cell therapy in B-cell acute lymphoblastic leukemia
Tác giả: Aïda Falgàs, Rodrigo Lázaro-Gorines, Carla Panisello, Talía Velasco-Hernandez, Andrea Mayado, Alba Pérez-Pons, Eulalia Genesca, Josep-Maria Ribera, Jordi Ribera, Mireia Camos, Manuel Ramírez-Orellana, Eduardo Anguita, Samanta Romina Zanetti, Paola Ballerini, José Luis Fuster, Manel Juan, Europa Azucena Azucena González-Navarro, Franco Locatelli, Ronald W W Stam, Sergio Querol, Pablo Velasco, Valentín Ortiz-Maldonado, Nuria Martínez-Cibrian, Laura Rubio-Pérez, Julio Delgado, Alberto Orfao, Luis Alvarez-Vallina, Clara Bueno, Pablo Menendez, Alba Martinez-Moreno, Meritxell Vinyoles, Mercedes Guerrero-Murillo, Narcís Fernandez-Fuentes, Heleia Roca-Ho, Néstor Tirado
Xuất bản: United States: Blood , 2025
Bộ sưu tập: NCBI
ddc:  305.90695
 
Lymphoid Malignancies in patients with Shwachman-Diamond Syndrome
Tác giả: Helen D Reed, Hyunwoo Do, Ian Atkinson, Katherine Coyne, Margret Joos, Sara Katherine Loveless, Sarah K Steltz, Leah Cheng, Maggie Malsch, Kasiani C Myers, Akiko Shimamura, Edie A Weller, Marian H Harris, Christopher R Reilly, Harrison K Tsai, Jason E Farrar, Bonnie W Lau, Lauren Pommert, Christopher J Gamper
Xuất bản: United States: Blood , 2025
Bộ sưu tập: NCBI
ddc:  614.5112
 

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